Our dual vectors generate normal levels of expression in non-human primate retina
Atsena is leveraging a dual AAV vector approach in a preclinical program for MYO7A-associated Usher Syndrome (USH1B). Because the MYO7A cDNA is too long to fit in a single vector, it is split in half and each half is delivered via a separate AAV vector. Upon co-infection of cells with both vectors, the gene halves recombine to form full length MYO7A.
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